Exome sequencing identified a de novo frameshift pathogenic variant of CTBP1 in an extremely rare case of HADDTS
Hossein Jafari Khamirani, Sina Zoghi, Ali Saber Sichani, Mehdi Dianatpour, Sanaz Mohammadi, Kaoru Tabei, Seyed Alireza Dastgheib
Topics & Concepts
Frameshift mutationProbandExome sequencingSanger sequencingBiologyHypotoniaGeneticsMutationGeneNeurological diseases and metabolismConnective tissue disorders researchMetalloenzymes and iron-sulfur proteins