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The state-of-the-art of N-of-1 therapies and the IRDiRC N-of-1 development roadmap

Anneliene Hechtelt Jonker, Elena-Alexandra Tãtaru, Holm Graeßner, David Dimmock, Adam Jaffé, Gareth Baynam, James Davies, Shruti Mitkus, Oxana Iliach, Rich Horgan, Erika F. Augustine, Alison Bateman-House, Anna M.G. Pasmooij, Timothy W. Yu, Matthis Synofzik, Julie Douville, Larissa Lapteva, Philip J. Brooks, Daniel O’Connor, Annemieke Aartsma‐Rus

2024Nature Reviews Drug Discovery29 citationsDOI

Topics & Concepts

Drug developmentMedicineState (computer science)PharmacologyComputer scienceDrugAlgorithmCystic Fibrosis Research AdvancesEpilepsy research and treatmentGenetics and Neurodevelopmental Disorders
The state-of-the-art of N-of-1 therapies and the IRDiRC N-of-1 development roadmap | Litcius