QR-313, an Antisense Oligonucleotide, Shows Therapeutic Efficacy for Treatment of Dominant and Recessive Dystrophic Epidermolysis Bullosa: A Preclinical Study

Olivier Bornert, Marieke Hogervorst, Pauline Nauroy, Johannes Bischof, Jim Swildens, Ioannis Athanasiou, Sara F. Tufa, Douglas R. Keene, Dimitra Kiritsi, Stefan Hainzl, Eva M. Murauer, M. Peter Marinkovich, Gerard Platenburg, Ingrid Haußer, Verena Wally, Tita Ritsema, Ulrich Koller, Elisabeth M. Haisma, Alexander Nyström