Lentiviral vector ALS20 yields high hemoglobin levels with low genomic integrations for treatment of beta-globinopathies

Laura Breda, Valentina Ghiaccio, Naoto Tanaka, Danuta Jarocha, Yasuhiro Ikawa, Osheiza Abdulmalik, Alisa Dong, Carla Casu, Tobias Raabe, Xiaochuan Shan, Gwenn Danet-Desnoyers, Aoife Doto, J.K. Everett, Frederic D. Bushman, Enrico Radaelli, Charles A. Assenmacher, James C. Tarrant, Natalie Hoepp, Ryo Kurita, Yukio Nakamura, Virginia Guzikowski, Kim Smith‐Whitley, Janet L. Kwiatkowski, Stefano Rivella