Patient and parent oriented tools to assess health-related quality of life, activity of daily living and caregiver burden in SMA. Rome, 13 July 2019

Eugenio Mercuri, Sonia Messina, Jacqueline Montes, Francesco Muntoni, Valeria Sansone, Laura Antonaci, Matt Civitello, Giorgia Coratti, Mencía de Lemus, Roberto De Sanctis, Marcus Droege Avexis, Tina Duong, Richard S. Finkel, A. Frongia, Ksenija Gorni Roche, Chad Heatwole, Nicole Gusset, Erik Henricson, Anna Mayhew, Chiara Marchesi, Eugenio Mercuri, Sonia Messina, Jacqueline Montes, Francesco Muntoni, Amy Pasternak, Astrid Pechmann, Maria Carmela Pera, Ivana Rubino, Valeria Sansone, Mary Schroth, Dylan Trundell, Volker Straub