In Vitro and In Vivo Amenability to Migalastat in Fabry Disease
Malte Lenders, Franciska Stappers, Eva Brand
Abstract
amenability, the treating clinician has the responsibility to monitor clinical and laboratory features to verify clinical response.
Topics & Concepts
Fabry diseaseIn vivoIn vitroMedicineMutationComputational biologyDiseaseBioinformaticsBiologyGeneticsInternal medicineGeneLysosomal Storage Disorders ResearchCarbohydrate Chemistry and SynthesisTrypanosoma species research and implications