A new score combining compound muscle action potential (CMAP) amplitudes and motor score is predictive of motor outcome after AVXS-101 (Onasemnogene Abeparvovec) SMA therapy
Rémi Barrois, Christine Barnérias, E. Deladrière, V. Leloup-Germa, Brian Tervil, Frédérique Audic, C. Boulay, Claude Cancés, Pascal Cintas, Jean‐Baptiste Davion, Caroline Espil‐Taris, V. Manel, Yann Péréon, Julie Piarroux, S Roy, C. Vuillerot, Ulrike Walther‐Louvier, Isabelle Desguerre, Cyril Gitiaux
Topics & Concepts
Compound muscle action potentialCohortSMA*MedicineSpinal muscular atrophySittingInternal medicinePhysical medicine and rehabilitationPhysical therapyDiseaseElectrophysiologyPathologyCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchCardiac Structural Anomalies and RepairMuscle Physiology and Disorders