Efficacy and Safety of Intravitreal Gene Therapy for Leber Hereditary Optic Neuropathy Treated within 6 Months of Disease Onset
Nancy J. Newman, Patrick Yu‐Wai‐Man, Valério Carelli, Mark L. Moster, Valérie Biousse, Catherine Vignal, Robert C. Sergott, Thomas Klopstock, Alfredo A. Sadun, Piero Barboni, Adam A. DeBusk, Jean‐François Girmens, Günther Rudolph, Rustum Karanjia, Magali Taiel, Laure Blouin, Gerard Smits, Barrett Katz, José‐Alain Sahel, Catherine Vignal, Rabih Hage, Claudia B. Catarino, Claudia Priglinger, Siegfried Priglinger, Stephan Thurau, Bettina von Livonius, Daniel Rudolf Muth, Armin Wolf, Jasmina Al-Tamami, Angelika Pressler, Cosima Schertler, Martin Hildebrandt, Michael Neuenhahn, Gad Heilweil, Irena Tsui, G. Baker Hubbard, Andrew Hendrick, Michael Dattilo, Jason H. Peragallo, Eman Hawy, Med Lindreth DuBois, Deborah Gibbs, Alcides Fernandes Filho, Jannah Dobbs, Michele Carbonelli, Lidia Di Vito, Manuela Contin, Susan Mohamed, Chiara La Morgia, Sara Silvestri, James Acheson, Maria Eleftheriadou, Simona Esposti, Maria Gemenetzi, Lauren Leitch-Devlin, William Tucker, Neringa Jurkutė, Melissa SantaMaria, Heather Tollis, Julie A. Haller, Maria Massini