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Small Molecule Inhibitors of Lymphocyte Perforin as Focused Immunosuppressants for Infection and Autoimmunity

Julie A. Spicer, Kristiina M. Huttunen, Jiney Jose, Ivo Dimitrov, Hedieh Akhlaghi, Vivien R. Sutton, Ilia Voskoboinik, Joseph A. Trapani

2022Journal of Medicinal Chemistry13 citationsDOIOpen Access PDF

Abstract

proof-of-concept experiments performed in mouse models of perforin-mediated immune pathologies that provide a potential pathway toward a clinically useful therapeutic agent.

Topics & Concepts

PerforinCTL*Immune systemImmunologyGranzymeAutoimmunityCytotoxic T cellBiologyCD8In vitroBiochemistryAutoimmune and Inflammatory Disorders ResearchAcute Lymphoblastic Leukemia researchChildhood Cancer Survivors' Quality of Life
Small Molecule Inhibitors of Lymphocyte Perforin as Focused Immunosuppressants for Infection and Autoimmunity | Litcius