Litcius/Paper detail

Using mechanistic models to support development of complex generic drug products: European Medicines Agency perspective

Efthymios Manolis, Alfredo García‐Arieta, Anders Lindahl, Evangelos Kotzagiorgis, Jobst Limberg, Øyvind Holte, Paulo Paixão, Carolien Versantvoort, Flora Musuamba Tshinanu, Kevin Blake, Michiel van den Heuvel

2023CPT Pharmacometrics & Systems Pharmacology18 citationsDOIOpen Access PDF

Abstract

Model-informed drug development (MIDD) approaches receive wide regulatory acceptance in the European Medicines Agency (EMA) to support new drug development. For generic drugs, the European regulators have not reached a common position on how to use these methods. This commentary expands on the existing EMA regulatory framework for bioequivalence and physiological based pharmacokinetic (PBPK) modeling to propose conditions where mechanistic models could support or potentially waive clinical bioequivalence (BE)/bioavailability (BA) studies.

Topics & Concepts

BioequivalenceAgency (philosophy)Regulatory sciencePhysiologically based pharmacokinetic modellingDrug developmentRegulatory agencyPerspective (graphical)DrugPharmacologyRisk analysis (engineering)Drug approvalBioavailabilityManagement scienceBusinessPharmacokineticsMedicineComputer sciencePolitical scienceEconomicsPublic administrationSociologyArtificial intelligencePathologySocial scienceComputational Drug Discovery MethodsViral Infectious Diseases and Gene Expression in InsectsInnovative Microfluidic and Catalytic Techniques Innovation