Inhibition of phosphodiesterase-4D in adults with fragile X syndrome: a randomized, placebo-controlled, phase 2 clinical trial
Elizabeth Berry‐Kravis, Mark Harnett, Scott A. Reines, Melody Reese, Lauren E. Ethridge, Abigail H. Outterson, Claire Michalak, Jeremiah Furman, Mark E. Gurney
Topics & Concepts
PlaceboTolerabilityCognitionRating scaleEffects of sleep deprivation on cognitive performanceFragile X syndromeRandomized controlled trialMedicineAudiologyClinical psychologyPsychologyPhysical therapyPediatricsAdverse effectPsychiatryInternal medicineDevelopmental psychologyPathologyAlternative medicineGenetics and Neurodevelopmental DisordersAutism Spectrum Disorder ResearchPeptidase Inhibition and Analysis