Endocrine dysfunction in adrenoleukodystrophy
Marc Engelen, Stephan Kemp, Florian Eichler
Topics & Concepts
AdrenoleukodystrophyLeukodystrophyMedicineMyelopathyHematopoietic stem cell transplantationTransplantationPathologyInternal medicineEndocrinologyDiseasePeroxisomeSpinal cordPsychiatryReceptorPeroxisome Proliferator-Activated ReceptorsMetabolism and Genetic DisordersAdipose Tissue and Metabolism