Litcius/Paper detail

CRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid Biobank

Maarten H. Geurts, Eyleen de Poel, Gimano D. Amatngalim, Rurika Oka, Fleur Michelle Meijers, Evelien Kruisselbrink, Peter van Mourik, Gitte Berkers, Karin M. de Winter‐de Groot, Sabine Michel, Danya Muilwijk, Bente L. Aalbers, Jasper Mullenders, Sylvia F. Boj, Sylvia W.F. Suen, Jesse E. Brunsveld, Hettie M. Janssens, Marcus Mall, Simon Y. Graeber, Ruben van Boxtel, Cornelis K. van der Ent, Jeffrey M. Beekman, Hans Clevers

2020Cell stem cell221 citationsDOIOpen Access PDF

Topics & Concepts

OrganoidCRISPRBiobankBiologyComputational biologyGenome editingGeneticsGenomeNonsense mutationCystic fibrosisMutationGeneMissense mutationCRISPR and Genetic EngineeringCystic Fibrosis Research AdvancesPluripotent Stem Cells Research