CRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid Biobank
Maarten H. Geurts, Eyleen de Poel, Gimano D. Amatngalim, Rurika Oka, Fleur Michelle Meijers, Evelien Kruisselbrink, Peter van Mourik, Gitte Berkers, Karin M. de Winter‐de Groot, Sabine Michel, Danya Muilwijk, Bente L. Aalbers, Jasper Mullenders, Sylvia F. Boj, Sylvia W.F. Suen, Jesse E. Brunsveld, Hettie M. Janssens, Marcus Mall, Simon Y. Graeber, Ruben van Boxtel, Cornelis K. van der Ent, Jeffrey M. Beekman, Hans Clevers
Topics & Concepts
OrganoidCRISPRBiobankBiologyComputational biologyGenome editingGeneticsGenomeNonsense mutationCystic fibrosisMutationGeneMissense mutationCRISPR and Genetic EngineeringCystic Fibrosis Research AdvancesPluripotent Stem Cells Research