Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy
Samuele Ferrari, Erika Valeri, Anastasia Conti, Serena Scala, Annamaria Aprile, Raffaella Di Micco, Anna Kajaste‐Rudnitski, Eugenio Montini, Giuliana Ferrari, Alessandro Aiuti, Luigi Naldini
Topics & Concepts
BiologyGenetic enhancementHaematopoiesisProgenitor cellScope (computer science)Computational biologyStem cellGene transferGeneHematopoietic stem cellGenome editingBioinformaticsCell biologyGeneticsCRISPRComputer scienceProgramming languageCRISPR and Genetic EngineeringVirus-based gene therapy researchViral gastroenteritis research and epidemiology