Trametinib for Refractory Chylous Effusions and Systemic Complications in Children with Noonan Syndrome
Taizo A. Nakano, Alexander W. Rankin, Aparna Annam, Ann M. Kulungowski, Leslie McCallen, Lauren R. S. Hill, Kathryn C. Chatfield
Topics & Concepts
MedicineNoonan syndromeTrametinibMEK inhibitorInternal medicineDosingMAPK/ERK pathwayOncologyKinaseBiologyCell biologyProtein Tyrosine PhosphatasesPI3K/AKT/mTOR signaling in cancerDermatological and Skeletal Disorders