Precision medicine for rare diseases: The times they are A-Changin'
Margarida D. Amaral
Topics & Concepts
Orphan drugDiseaseIntensive care medicineMedicinePrecision medicineRepurposingPopulationBiomedicineAffect (linguistics)Drug repositioningDrugRisk analysis (engineering)BioinformaticsPharmacologyPsychologyPathologyBiologyEnvironmental healthCommunicationEcologyCystic Fibrosis Research AdvancesGenomics and Rare DiseasesImmunodeficiency and Autoimmune Disorders