The potential of gene editing for Huntington’s disease
Wenzhen Duan, Ece Urani, Mark P. Mattson
Topics & Concepts
CRISPRHuntington's diseaseHuntingtinGenome editingBiologyTrinucleotide repeat expansionCas9GeneNeuroscienceHuntingtin ProteinGeneticsGene knockinGenetic enhancementDiseaseMutantAlleleMedicinePathologyCRISPR and Genetic EngineeringGenetic Neurodegenerative DiseasesGenetics, Aging, and Longevity in Model Organisms