RNA-targeting strategies as a platform for ocular gene therapy
Satheesh Kumar, Lewis E. Fry, Jiang-Hui Wang, Keith R. Martin, Alex W. Hewitt, Fred K. Chen, Guei‐Sheung Liu
Topics & Concepts
CRISPRRNA interferenceComputational biologyRNAGenome editingBiologyGenetic enhancementCas9Personalized medicineBioinformaticsMedicineGeneGeneticsCRISPR and Genetic EngineeringAdvanced biosensing and bioanalysis techniquesRNA Interference and Gene Delivery