Potent and uniform fetal hemoglobin induction via base editing
Thiyagaraj Mayuranathan, Gregory A. Newby, Ruopeng Feng, Yu Yao, Kalin Mayberry, Cícera R. Lazzarotto, Yichao Li, Rachel M. Levine, Nikitha Nimmagadda, Erin Dempsey, Guolian Kang, Shaina N. Porter, Phillip A. Doerfler, Jingjing Zhang, Yoonjeong Jang, Jingjing Chen, Henry W. Bell, Merlin Crossley, Senthil Velan Bhoopalan, Akshay Sharma, John F. Tisdale, Shondra M. Pruett‐Miller, Yong Cheng, Shengdar Q. Tsai, David R. Liu, Mitchell J. Weiss, Jonathan Yen
Topics & Concepts
BiologyFetal hemoglobinHemoglobinFetusComputational biologyGeneticsPregnancyBiochemistryHemoglobinopathies and Related DisordersPrenatal Screening and DiagnosticsNeonatal Health and Biochemistry