Immune function in X-linked retinoschisis subjects in an AAV8-RS1 phase I/IIa gene therapy trial
Alaknanda Mishra, Camasamudram Vijayasarathy, Catherine A. Cukras, Henry E. Wiley, H. Nida Sen, Yong Zeng, Lisa L. Wei, Paul A. Sieving
Topics & Concepts
Immune systemGenetic enhancementMedicineImmunologyVirologyBiologyGeneGeneticsVirus-based gene therapy researchRetinal Development and DisordersRNA Interference and Gene Delivery