Beyond current treatment of Fanconi Anemia: What do advances in cell and gene-based approaches offer?
Elena Martínez‐Balsalobre, Jean-Hugues Guervilly, Jenny van Asbeck-van der Wijst, Ana B. Pérez‐Oliva, Christophe Lachaud
Topics & Concepts
Fanconi anemiaGenome editingStem cellGenetic enhancementBiologyDiseaseHaematopoiesisInduced pluripotent stem cellCRISPRCancer researchBone marrow failureHematopoietic stem cell transplantationImmunologyGeneDNA repairMedicineGeneticsEmbryonic stem cellPathologyCRISPR and Genetic EngineeringDNA Repair MechanismsChromosomal and Genetic Variations