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Hearing of Otof-deficient mice restored by trans-splicing of N- and C-terminal otoferlin

Honghai Tang, Hui Wang, Shengyi Wang, Shao Wei Hu, Jun Lv, Mengzhao Xun, Kaiyu Gao, Fang Wang, Yuxin Chen, Daqi Wang, Wuqing Wang, Huawei Li, Yilai Shu

2022Human Genetics83 citationsDOI

Topics & Concepts

BiologyAuditory neuropathyTransduction (biophysics)GeneGeneticsHearing lossAudiologyBiochemistryMedicineRNA regulation and diseaseCRISPR and Genetic EngineeringHearing, Cochlea, Tinnitus, Genetics
Hearing of Otof-deficient mice restored by trans-splicing of N- and C-terminal otoferlin | Litcius