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Truncated titin proteins in dilated cardiomyopathy

Quentin McAfee, Yingxian Chen, Yifan Yang, Matthew A. Caporizzo, Michael P. Morley, Apoorva Babu, Sunhye Jeong, Jeffrey Brandimarto, Kenneth Bedi, Emily Flam, Joseph Cesare, Thomas P. Cappola, Kenneth B. Margulies, Benjamin L. Prosser, Zoltàn Arany

2021Science Translational Medicine69 citationsDOIOpen Access PDF

Abstract

DCM hearts, and support combined dominant-negative and haploinsufficiency contributions to disease.

Topics & Concepts

TitinObscurinDilated cardiomyopathyHaploinsufficiencyCardiomyopathyBiologyMolecular biologyContractilityBlotCell biologySarcomereGeneticsMedicineMyocyteInternal medicineHeart failureEndocrinologyGenePhenotypeCardiomyopathy and Myosin StudiesViral Infections and Immunology ResearchRNA and protein synthesis mechanisms
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