Litcius/Paper detail

Applications of Gene Therapy in Cardiomyopathies

Alessia Argirò, Quan M. Bui, Kimberly N. Hong, Enrico Ammirati, Iacopo Olivotto, Eric Adler

2023JACC Heart Failure53 citationsDOI

Topics & Concepts

Genetic enhancementMedicineAdeno-associated virusClinical trialGene deliveryDuchenne muscular dystrophyGeneCardiomyopathyDiseaseHypertrophic cardiomyopathyBioinformaticsHeart failurePathologyGeneticsInternal medicineBiologyVector (molecular biology)Recombinant DNACRISPR and Genetic EngineeringViral Infections and Immunology ResearchVirus-based gene therapy research