Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy
Tolulope O. Rosanwo, Daniel E. Bauer
Topics & Concepts
Ex vivoHemoglobinopathyGenetic enhancementBiologyGeneGeneticsMedicineIn vivoHemolytic anemiaImmunologyCRISPR and Genetic EngineeringPluripotent Stem Cells ResearchHemoglobinopathies and Related Disorders