Abatacept for treatment-refractory pediatric CTLA4-haploinsufficiency
Anna-Lisa Lanz, Martin Bernhard Riester, Philipp Peters, Tobias Schwerd, Eberhard Lurz, Mohammad Hajji, Meino Rohlfs, Julia Ley‐Zaporozhan, Christoph Walz, Daniel Kotlarz, Christoph Klein, Michael H. Albert, Fabian Hauck
Topics & Concepts
AbataceptHaploinsufficiencyMedicineRefractory (planetary science)Immune dysregulationInternal medicineImmunologyRituximabDiseaseAntibodyGenePhysicsBiochemistryPhenotypeChemistryAstrobiologyImmunodeficiency and Autoimmune DisordersBlood disorders and treatmentsPlatelet Disorders and Treatments