NMNAT2 is downregulated in glaucomatous RGCs, and RGC-specific gene therapy rescues neurodegeneration and visual function
Fang Fang, Pei Zhuang, Xue Feng, Pingting Liu, Dong Liu, Haoliang Huang, Liang Li, Wei Chen, Liang Liu, Yang Sun, Haowen Jiang, Jiangbin Ye, Yang Hu
Topics & Concepts
NeurodegenerationBiologyFunction (biology)NeuroscienceGenetic enhancementGeneGeneticsMedicineInternal medicineDiseaseGlaucoma and retinal disordersRetinal Development and DisordersRetinal Diseases and Treatments