Litcius/Paper detail

A physiologically-based pharmacokinetic model to describe antisense oligonucleotide distribution after intrathecal administration

Michael Monine, Daniel A. Norris, Yanfeng Wang, Ivan Nestorov

2021Journal of Pharmacokinetics and Pharmacodynamics60 citationsDOI

Topics & Concepts

PharmacokineticsSpinal muscular atrophyMedicineNeurosciencePharmacologyIntrathecalAmyotrophic lateral sclerosisCentral nervous systemDistribution (mathematics)Spinal cordBiologyPathologyAnesthesiaDiseaseMathematicsMathematical analysisNeurogenetic and Muscular Disorders ResearchAmyotrophic Lateral Sclerosis ResearchRNA Interference and Gene Delivery
A physiologically-based pharmacokinetic model to describe antisense oligonucleotide distribution after intrathecal administration | Litcius