Novel use of nusinersen as a therapeutic bridge to onasemnogene abeparvovec‐xioi in a premature neonate with type 1 spinal muscular atrophy
Leah Ferrante, Alexandria E. Melendez‐Zaidi, Wilfreda Lindsey, Timothy Lotze
Topics & Concepts
Pediatric NeurologyNeurologyMedicinePediatricsPsychologyFamily medicinePsychiatryNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal SurgeryCardiac Structural Anomalies and Repair