Discovering C3 targeting therapies for paroxysmal nocturnal hemoglobinuria: Achievements and pitfalls
Antonio M. Risitano, Régis Peffault de Latour, Luana Marano, Camilla Frieri
Topics & Concepts
Paroxysmal nocturnal hemoglobinuriaEculizumabMedicineHemolysisHemoglobinuriaComplement systemImmunologyInternal medicinePharmacologyAntibodyComplement system in diseasesAdenosine and Purinergic SignalingCoagulation, Bradykinin, Polyphosphates, and Angioedema