Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations

Kalyan Dulla, Ralph Slijkerman, Hester C. van Diepen, Sílvia Albert, Margo Dona, Wouter Beumer, Janne J. Turunen, Hee Lam Chan, Iris A. Schulkens, Lars Vorthoren, Cathaline den Besten, Levi C.M. Buil, Iris Schmidt, Jiayi Miao, Hanka Venselaar, Jingjing Zang, Stephan C. F. Neuhauss, Theo Peters, Sanne Broekman, Ronald J. E. Pennings, Hannie Kremer, Gerard Platenburg, Peter Adamson, Erik de Vrieze, Erwin van Wijk