Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR
Jasmina Cehajic‐Kapetanovic, Kanmin Xue, Cristina Martínez-Fernández de la Cámara, Anika Nanda, Alexandra Davies, Laura J. Taylor, Anna Paola Salvetti, M. Dominik Fischer, James Aylward, Alun R. Barnard, Jasleen K. Jolly, Edmond Luo, Brandon J. Lujan, Tuyen Ong, Aniz Girach, Graeme C. Black, Ninel Z. Gregori, Janet L. Davis, Potyra R. Rosa, Andrew Lotery, Byron L. Lam, Paulo Stanga, Robert E. MacLaren
Topics & Concepts
Retinitis pigmentosaMicroperimetryMedicineClinical endpointGenetic enhancementRetinal degenerationRetinalVisual acuityOphthalmologyClinical trialInternal medicineGeneBiologyGeneticsRetinal Development and DisordersRetinal Diseases and TreatmentsAdvanced Fluorescence Microscopy Techniques