Litcius/Paper detail

Gene Therapy for Cystic Fibrosis: Lessons Learned and Paths Forward

Soon Ho Choi, John F. Engelhardt

2021Molecular Therapy23 citationsDOIOpen Access PDF

Topics & Concepts

Genetic enhancementCystic fibrosisCystic fibrosis transmembrane conductance regulatorGene deliveryApical membraneMedicineBiologyLungImmunologyGenePathologyInternal medicineEpitheliumGeneticsCystic Fibrosis Research AdvancesNeonatal Respiratory Health ResearchRespiratory viral infections research