Long-term safety and outcomes in hereditary tyrosinaemia type 1 with nitisinone treatment: a 15-year non-interventional, multicentre study
Ute Spiekerkoetter, María L. Couce, Anibh M. Das, Corinne De Laet, Carlo Dionisi‐Vici, Allan M. Lund, Manuel Schiff, Marco Spada, Erik Sparve, Johan Szamosi, Roshni Vara, Mattias Rudebeck
Topics & Concepts
MedicineTerm (time)Internal medicinePhysicsQuantum mechanicsMetabolism and Genetic DisordersBiomedical Research and Pathophysiologymelanin and skin pigmentation