Comprehensive transcriptome-wide analysis of spliceopathy correction of myotonic dystrophy using CRISPR-Cas9 in iPSCs-derived cardiomyocytes
Sumitava Dastidar, Debanjana Majumdar, Jaitip Tipanee, Kshitiz Singh, Arnaud F. Klein, Denis Furling, Marinee Chuah, Thierry VandenDriessche
Topics & Concepts
CRISPRMyotonic dystrophyTranscriptomeInduced pluripotent stem cellBiologyComputational biologyGeneticsGeneGene expressionEmbryonic stem cellGenetic Neurodegenerative DiseasesMitochondrial Function and PathologyCRISPR and Genetic Engineering