Systematic screening identifies therapeutic antisense oligonucleotides for Hutchinson–Gilford progeria syndrome
M. Puttaraju, Michaela Jackson, Stéphanie Klein, Asaf Shilo, C. Frank Bennett, Leslie B. Gordon, Frank Rigo, Tom Misteli
Topics & Concepts
ProgeriaLMNABiologyIn vivoRNA splicingOligonucleotideCell biologyCancer researchRNAGeneticsGeneMutationNuclear Structure and FunctionRNA Research and SplicingDNA Repair Mechanisms