Litcius/Paper detail

Restoration of dystrophin expression in mice by suppressing a nonsense mutation through the incorporation of unnatural amino acids

Ningning Shi, Qi Yang, Haoran Zhang, Jiaqi Lü, Haishuang Lin, Yang Xu, A. Abulimiti, Jialu Cheng, Yu Wang, Le Tong, Tianchang Wang, Xiaodong Zhang, Hongmin Chen, Qing Xia

2021Nature Biomedical Engineering50 citationsDOI

Topics & Concepts

Nonsense mutationAmino acidDystrophinTransfer RNABiologyDuchenne muscular dystrophyAminoacyl tRNA synthetaseStop codonMutationGeneNonsenseMolecular biologyGeneticsBiochemistryChemistryRNAMissense mutationRNA and protein synthesis mechanismsRNA modifications and cancerRNA Research and Splicing