Litcius/Paper detail

Core data set on safety, efficacy, and durability of hemophilia gene therapy for a global registry: Communication from the SSC of the ISTH

Barbara A. Konkle, Glen Pierce, Donna Coffin, Mayss Naccache, R. Cary Clark, Lindsey A. George, Alfonso Iorio, Brian O’Mahony, Steven W. Pipe, Mark W. Skinner, Crystal Watson, Flora Peyvandi, Johnny Mahlangu

2020Journal of Thrombosis and Haemostasis48 citationsDOIOpen Access PDF

Topics & Concepts

MedicineClinical trialObservational studyQuality of life (healthcare)Intensive care medicineFamily medicineInternal medicineNursingHemophilia Treatment and ResearchVirus-based gene therapy researchNeurogenetic and Muscular Disorders Research
Core data set on safety, efficacy, and durability of hemophilia gene therapy for a global registry: Communication from the SSC of the ISTH | Litcius