Litcius/Paper detail

Congenital myasthenic syndromes: where do we go from here?

Sithara Ramdas, David Beeson

2021Neuromuscular Disorders50 citationsDOI

Topics & Concepts

Neuromuscular transmissionCongenital myasthenic syndromeGeneMyasthenia gravisNeuromuscular junctionPhenotypeNeuromuscular diseaseTransmission (telecommunications)MedicineLoss functionDiseaseBioinformaticsGenetic heterogeneityGeneticsBiologyMutationNeuroscienceImmunologyInternal medicineElectrical engineeringEngineeringMyasthenia Gravis and ThymomaCellular transport and secretionGenomics and Rare Diseases