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A scalable organoid model of human autosomal dominant polycystic kidney disease for disease mechanism and drug discovery

Tracy Tran, Cheng Song, Trang Nguyen, Shun-Yang Cheng, Jill A. McMahon, Rui Yang, Qiuyu Guo, Bálint Dér, Nils O. Lindström, Daniel C.-H. Lin, Andrew P. McMahon

2022Cell stem cell129 citationsDOIOpen Access PDF

Topics & Concepts

OrganoidBiologyDrug discoveryDiseaseMechanism (biology)Polycystic kidney diseaseComputational biologyDrugBioinformaticsKidneyNeurosciencePharmacologyGeneticsInternal medicineMedicineEpistemologyPhilosophyRenal and related cancersGenetic and Kidney Cyst DiseasesRenal cell carcinoma treatment
A scalable organoid model of human autosomal dominant polycystic kidney disease for disease mechanism and drug discovery | Litcius