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The Miami Framework for ALS and related neurodegenerative disorders: an integrated view of phenotype and biology

Michael Benatar, Joanne Wuu, Edward D. Huey, Corey T. McMillan, Ronald C. Petersen, Ronald B. Postuma, Caroline McHutchison, Laynie Dratch, Jalayne J. Arias, Anita Crawley, Henry Houlden, Michael McDermott, Xueya Cai, Neil Thakur, Adam L. Boxer, Howard J. Rosen, Bradley F. Boeve, Penny A. Dacks, Stephanie Cosentino, Sharon Abrahams, Neil A. Shneider, Paul Lingor, Jeremy M. Shefner, Peter M. Andersen, Ammar Al‐Chalabi, Martin R. Turner, Attendees of the Second International Pre-Symptomatic ALS Workshop, Ronald C. Petersen, Peggy Allred, Stanley H. Appel, David Benatar, James D. Berry, Meg Bradbury, Lucie Bruijn, Jennifer Buczyner, Nathan Carberry, James B. Caress, Thomas H. Champney, Kuldip D. Dave, Stephanie Fradette, Volkan Granit, Anne‐Laure Grignon, Amelie K. Gubitz, Matthew B. Harms, Terry Heiman‐Patterson, Sharon Hesterlee, Karen A. Lawrence, Travis “Pete” Lewis, Oren Levy, Tahseen Mozaffar, Christine Stanislaw, Alexander G. Thompson, Olga Uspenskaya, Patrick Weydt, Lorne Zinman

2024Nature Reviews Neurology41 citationsDOIOpen Access PDF

Topics & Concepts

Frontotemporal dementiaAmyotrophic lateral sclerosisNeurodegenerationDiseaseNeurosciencePhenotypeBiomarkerEndophenotypeProdromeC9orf72DementiaClinical phenotypeMedicineBioinformaticsPsychologyBiologyPathologyGeneticsPsychiatryCognitionPsychosisGeneAmyotrophic Lateral Sclerosis ResearchParkinson's Disease Mechanisms and TreatmentsAlzheimer's disease research and treatments
The Miami Framework for ALS and related neurodegenerative disorders: an integrated view of phenotype and biology | Litcius