Recommendations on hematopoietic stem cell transplantation for patients with Diamond–Blackfan anemia. On behalf of the Pediatric Diseases and Severe Aplastic Anemia Working Parties of the EBMT
Cristina Díaz de Heredia, Dorine Bresters, Lawrence Faulkner, Akif Yeşilipek, Brigitte Strahm, Maurizio Miano, Jean‐Hugues Dalle, Régis Peffault de Latour, Selim Corbacioglu
Topics & Concepts
MedicineDiamond–Blackfan anemiaHematopoietic stem cell transplantationAplastic anemiaStem cellTransplantationSavior siblingPediatricsDiseaseAnemiaOncologyInternal medicineBone marrowGeneRNARibosomeGeneticsBiochemistryChemistryBiologyHemoglobinopathies and Related DisordersEpigenetics and DNA MethylationRNA modifications and cancer