Laboratory-Scale Lentiviral Vector Production and Purification for Enhanced Ex Vivo and In Vivo Genetic Engineering
Monica Soldi, Lucia Sergi Sergi, Giulia Unali, Thomas Kerzel, Ivan Cuccovillo, Paola Capasso, Andrea Annoni, Mauro Biffi, Paola M. V. Rancoita, Alessio Cantore, Angelo Lombardo, Luigi Naldini, Mario Leonardo Squadrito, Anna Kajaste‐Rudnitski
Abstract
as compared to TU-matched, laboratory-grade vectors. Our results highlight the value of accessible purified LV production for experimental studies and preclinical testing.
Topics & Concepts
Ex vivoIn vivoProgenitor cellBiologyGenetic enhancementViral vectorComputational biologyStem cellRecombinant DNAGeneCell biologyBiotechnologyGeneticsVirus-based gene therapy researchRNA Interference and Gene DeliveryCRISPR and Genetic Engineering