Gene Therapy for Hemoglobinopathies
Alexis Leonard, John F. Tisdale, Melissa Bonner
Topics & Concepts
Genetic enhancementMedicineThalassemiaDiseaseHematopoietic stem cell transplantationClinical trialIntensive care medicineTransplantationGenome editingGeneInternal medicineBiologyGeneticsGenomeCRISPR and Genetic EngineeringVirus-based gene therapy researchHemoglobinopathies and Related Disorders