Trofinetide Treatment Demonstrates a Benefit Over Placebo for the Ability to Communicate in Rett Syndrome
Jeffrey L. Neul, Alan K. Percy, Tim A. Benke, Elizabeth Berry‐Kravis, Daniel G. Glaze, Sarika U. Peters, Eric D. Marsh, Di An, Kathie M. Bishop, James M. Youakim
Topics & Concepts
PlaceboRett syndromeChecklistConfidence intervalPsychologySignificant differenceMean differenceRandomized controlled trialAudiologyMedicineClinical psychologyDevelopmental psychologyInternal medicineCognitive psychologyPathologyAlternative medicineBiochemistryGeneChemistryGenetics and Neurodevelopmental DisordersFamily and Disability Support ResearchNeurogenetic and Muscular Disorders Research