Sirolimus treatment for tuberous sclerosis complex prior to epilepsy: Evidence from a registry-based real-world study
Yan-Wen Shen, Yang‐Yang Wang, Mengna Zhang, Yong Xu, Qian Lu, Wen He, Huimin Chen, Liying Liu, Ling-Yu Pang, Qiuhong Wang, Shuo Dun, Yufen Li, Jing Gao, Fang Han, Li‐Ping Zou
Topics & Concepts
Tuberous sclerosisSirolimusMedicineCohortEpilepsyPediatricsClinical endpointRandomized controlled trialInternal medicinePsychiatryTuberous Sclerosis Complex ResearchEpilepsy research and treatmentPI3K/AKT/mTOR signaling in cancer