Sirolimus for treatment of patients with inclusion body myositis: a randomised, double-blind, placebo-controlled, proof-of-concept, phase 2b trial
Olivier Benvéniste, Jean‐Yves Hogrel, Lisa Belin, M. Annoussamy, Damien Bachasson, Aude Rigolet, Pascal Laforêt, Gaëlle Dzangué-Tchoupou, Joe‐Elie Salem, Lee S. Nguyen, Tanya Stojkovic, Noël Zahr, B. Hervier, Océane Landon‐Cardinal, Anthony Béhin, Edith Guilloux, Harmen Reyngoudt, Damien Amelin, Akinori Uruha, K. Mariampillai, Benjamin Marty, B. Eymard, Jean‐Sébastien Hulot, Steven A. Greenberg, Pierre G. Carlier, Yves Allenbach
Topics & Concepts
Double blindPlaceboProof of conceptMedicineInclusion body myositisPhase (matter)Physical therapyInternal medicineMyositisAlternative medicineComputer sciencePathologyPhysicsQuantum mechanicsOperating systemInflammatory Myopathies and DermatomyositisSpondyloarthritis Studies and TreatmentsMuscle and Compartmental Disorders