Advances in the Therapy of Spinal Muscular Atrophy
Jenna Klotz, Carolina Tesi Rocha, Sally Dunaway Young, Tina Duong, MyMy C. Buu, Jacinda B. Sampson, John Day
Topics & Concepts
Spinal muscular atrophySMA*MedicineNatural historyDiseasePhysical medicine and rehabilitationPhysical therapyPathologyIntensive care medicinePediatricsInternal medicineCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery