Current treatment options and novel nanotechnology-driven enzyme replacement strategies for lysosomal storage disorders
Ambra Del Grosso, Gabriele Parlanti, Roberta Mezzena, Marco Cecchini
Topics & Concepts
Enzyme replacement therapyMedicineFabry diseaseSubstrate reduction therapyLysosomal storage disordersDiseaseNeurosciencePathologyBiologyLysosomal Storage Disorders ResearchBiomedical Research and PathophysiologyCellular transport and secretion