Prospects for gene replacement therapies in amyotrophic lateral sclerosis
Ilaria Giovannelli, Adrian Higginbottom, Janine Kirby, Mimoun Azzouz, Pamela J. Shaw
Topics & Concepts
Amyotrophic lateral sclerosisRiluzoleMedicineDiseaseSpinal muscular atrophyLoss functionGenetic enhancementSMN1NeuroscienceBioinformaticsGenePathologyBiologyGeneticsPhenotypeNeurogenetic and Muscular Disorders ResearchAmyotrophic Lateral Sclerosis ResearchAutism Spectrum Disorder Research